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Intronic CRISPR Repair in a Preclinical Model of Noonan Syndrome–Associated Cardiomyopathy
ISSN
0009-7322
Date Issued
2020
Author(s)
Hanses, Ulrich
Kleinsorge, Mandy
Roos, Lennart
Barbarics, Boris
El-Battrawy, Ibrahim
Lan, Huan
Hindmarsh, Robin
Diecke, Sebastian
Adham, Ibrahim
Altmüller, Janine
Nürnberg, Peter
DOI
10.1161/CIRCULATIONAHA.119.044794